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Barth Syndrome

Showing 1 - 25 of >10,000

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Barth Syndrome Trial in Baltimore (Elamipretide)

Completed
  • Barth Syndrome
  • Baltimore, Maryland
    McKusick-Nathans Institute of Genetic Medicine, Johns Hopkins Un
Mar 7, 2022

Mitochondrial Diseases, Barth Syndrome Trial (elamipretide)

Available
  • Mitochondrial Diseases
  • Barth Syndrome
  • (no location specified)
Nov 1, 2021

Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency, Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2),

No longer available
  • Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency
  • +7 more
  • Pittsburgh, Pennsylvania
    University of Pittsburgh Division of Medical Genetics, Children'
Dec 8, 2021

Mitochondrial Diseases, Kearns-Sayre Syndrome, MIDD Trial in Austria, Germany, Italy

Recruiting
  • Mitochondrial Diseases
  • +17 more
    • Innsbruck, Austria
    • +18 more
    Sep 23, 2022

    Heart and Muscle Metabolism in Barth Syndrome

    Completed
    • Barth Syndrome
      • Saint Louis, Missouri
        Washington University
      May 29, 2020

      Barth Syndrome Trial in Saint Louis (Resistance exercise and protein supplementation)

      Completed
      • Barth Syndrome
      • Resistance exercise and protein supplementation
      • Saint Louis, Missouri
        Washington University
      May 11, 2020

      POTS - Postural Orthostatic Tachycardia Syndrome Trial in Malmö (Training program)

      Active, not recruiting
      • POTS - Postural Orthostatic Tachycardia Syndrome
      • Training program
      • Malmö, Sweden
        Skånes Universitetssjukhus Malmö, Department of Cardiology
      Dec 15, 2022

      Inherited Cardiac Arrythmias, Long QT Syndrome (LQTS), Brugada Syndrome (BrS) Trial in Baltimore

      Enrolling by invitation
      • Inherited Cardiac Arrythmias
      • +9 more
        • Baltimore, Maryland
          Johns Hopkins Medical Institute
        Jan 5, 2023

        Aicardi-Goutières Syndrome Trial in Edinburgh (Abacavir (ABC), Lamivudine (3TC), Abacavir (ABC)+Lamivudine (3TC)+Zidovudine

        Recruiting
        • Aicardi-Goutières Syndrome
        • Abacavir (ABC)
        • +2 more
        • Edinburgh, United Kingdom
          Yanick Crow
        Aug 26, 2022

        Scapholunate Advanced Collapse (SLAC), Scapholunate Crystalline Advanced Collapse (SCAC), Scaphoid, Trapezium, and Trapezoid

        Recruiting
        • Scapholunate Advanced Collapse (SLAC)
        • +10 more
        • KinematX total wrist arthroplasty system
        • Loma Linda, California
        • +4 more
        Jan 30, 2023

        Vineland II Scale of Long-term Development of Pyridoxine

        Not yet recruiting
        • Pyridoxine-Dependent Epilepsy
        • VINELAND II
        • Angers, France
          CHU Angers
        Sep 19, 2023

        POTS Trial in Malmö (Training program)

        Withdrawn
        • POTS
        • Training program
        • Malmö, Sweden
          Skånes Universitetssjukhus Malmö, Department of Cardiology
        Nov 23, 2021

        Vascular Health and Risk Factors in Children With Down Syndrome

        Recruiting
        • Down Syndrome
        • +2 more
        • Evaluate vascular disease risk factors in children with Down Syndrome
        • Determine the associations between cardiovascular disease risk factors and markers of early atherosclerosis in children with Down Syndrome
        • Salt Lake City, Utah
          University of Utah
        May 23, 2022

        Role of Novel ILR in the Management of PVCs

        Recruiting
        • PVC - Premature Ventricular Contraction
        • Myocarditis
        • Monitoring of patients presenting with PVCs
        • Overland Park, Kansas
        • +5 more
        Sep 27, 2023

        Carpal Tunnel, Carpal Tunnel Syndrome, Carpal Tunnel Syndrome Left Trial in Redwood City (Preference Elicitation tool)

        Enrolling by invitation
        • Carpal Tunnel
        • +4 more
        • Preference Elicitation tool
        • Redwood City, California
          Stanford Health Care
        Aug 4, 2022

        Neuroendocrine Tumors, Progesterone Receptor Positive Tumor, Estrogen Receptor Positive Tumor Trial in São Paulo (Tamoxifen)

        Active, not recruiting
        • Neuroendocrine Tumors
        • +2 more
        • Tampa, Florida
        • +1 more
        Jan 13, 2023

        Early Risk Stratification in ED Chest Pain Patients

        Completed
        • Acute Coronary Syndrome
        • Thrombolysis in myocardial infarction score
        • +2 more
        • Hong Kong, China
          Prince of Wales Hospital
        Apr 14, 2021

        Smoking, Acute Coronary Syndrome, Recurrence Trial in Monastir (procedure, drug, other)

        Completed
        • Smoking
        • +2 more
        • Nicotine replacement therapy delivred in cardiology intensive care unit versus Nicotine replacement therapy delivered after hospital discharge
        • +2 more
        • Monastir, Tunisia
          Abroug
        May 10, 2021

        Safety Issues Trial in Cali (Neonatal thymus transplantation)

        Recruiting
        • Safety Issues
        • Neonatal thymus transplantation
        • Cali, Valle Del Cauca, Colombia
          Fundación Valle Del Lili
        Dec 14, 2022

        Antibody-mediated Rejection, Lung Transplant Rejection Trial (Extracorporeal Photopheresis)

        Not yet recruiting
        • Antibody-mediated Rejection
        • Lung Transplant Rejection
        • Extracorporeal Photopheresis
        • (no location specified)
        Oct 30, 2023

        CT-based Myocardial Characterization (CTMyoC)

        Recruiting
        • Different Cardiomyopathy and Major Cardiovascular Adverse Events
          • Milano, Italy
            IRCCS San Raffaele
          Sep 1, 2023

          Stress Related Disorder, Nutrition, Healthy, Metabolism Trial in Bonn (Sleep Deprivation, Dexamethasone Supplementation)

          Recruiting
          • Stress Related Disorder
          • +2 more
          • Sleep Deprivation
          • Dexamethasone Supplementation
          • Bonn, North Rhine-Westphalia, Germany
            University Hospital Bonn, Department of Psychiatry and Psychothe
          Aug 24, 2023

          COVID-19, Critical Illness, Hypercytokinemia Trial in Ulm (Application of exosomes in a whole blood assay)

          Recruiting
          • COVID-19
          • +3 more
          • Application of exosomes in a whole blood assay
          • Ulm, Germany
            Ulm University Hospital, Clinic of Anesthesiology and Intensive
          Jan 17, 2022

          Nitric Oxide, COVID-19, Surgery Trial (Nitric Oxide Gas)

          Not yet recruiting
          • Nitric Oxide
          • +3 more
          • Nitric Oxide Gas
          • (no location specified)
          Feb 7, 2023

          Nephrotic Syndrome in Children Trial in China (Adrenocorticotrophic Hormone, Steroid)

          Recruiting
          • Nephrotic Syndrome in Children
          • Wuhan, Hubei, China
          • +7 more
          Oct 8, 2023